Genetics
News, opinions and meeting coverage in genetics.
Latest in Genetics
Phase III trial falls short of efficacy target, but positive signal emerges in younger kids
If approved, this would be the first drug for Niemann-Pick disease type C
This is the second time the drug has been submitted to the FDA for Niemann-Pick disease type C
In randomized study, guided site-specific therapy improved PFS versus empirical chemotherapy
This is the second time the drug has been submitted to the FDA for Niemann-Pick disease type C
In randomized study, guided site-specific therapy improved PFS versus empirical chemotherapy
More in Genetics
Studies show 90% reduction in intravitreal treatment burden, durable effect on vision, anatomy
![ASRS over a photo of Stockholmsmässan Convention Center in Stockholm, Sweden.](http://assets.medpagetoday.net/media/images/111xxx/111137.jpg)
U.S. clinics market oligonucleotide therapy for a wide range of conditions, without much evidence
![A computer rendering of an oligonucleotide aptamer attacking a cancer cell.](http://assets.medpagetoday.net/media/images/110xxx/110966.jpg)
Phase II study found brigatinib exceeded historical control by shrinking 10% of targeted tumors
![A computer rendering of a meningioma.](http://assets.medpagetoday.net/media/images/110xxx/110772.jpg)